U.S. regulator OKs 1st sickle cell drug in almost 20 years
Food and Drug Administration said Friday it has approved a drug called Endari to reduce severe complications associated with sickle cell disease in patients aged five years and older .
My honest advice to a sickle cell patient
Recently, I was resting at home, skimming through The Citizen newspaper. Then, suddenly I got a phone call from my colleague at work—Dr Haule.
A SMART Idea: Point-of-Care Diagnostic for Sickle Cell Disease and Malaria (Interview) |
Sickle cell disease and malaria are perhaps the biggest public health challenges in many parts of Africa. Countless organizations are tackling these two
What blood donation means to sickle-cell disease patients
Patients find themselves in desperate need, especially sickle-cell disease patients
Top Court in India Rejects Novartis Drug Patent
Production of cheap copycat drugs for H.I.V. and cancer used by people in developing countries in Africa and Asia was ensured on Monday in a ruling by India’s Supreme Court.
FDA Approves First Sickle Cell Drug in 20 Years
Approximately 100,000 people in the U.S. have the disorder
FDA Approves First New Sickle Cell Drug in Almost 20 Years
The US Food and Drug Administration (FDA) on Friday granted approval to Emmaus Medical’s Endari (L-glutamine oral powder), the first treatment approved for patients with sickle cell disease in almost 20 years.
Sickle Cell 101
A non-profit organization educating all people affected by sickle cell through the use of social media. Learn more about sickle cell today.
NIH must ensure sickle cell drug available at reasonable price, group says
NIH needs to secure commitments from drug companies to ensure that a potential cure for sickle cell is not priced out of reach, a group says.
A sickle cell drug reaches a critical readout. Here’s what you need to know
A late-stage clinical trial of Global Blood Therapeutics' sickle cell drug is nearing an interim but important readout before the end of the second quarter.
What is Sickle-Cell Disease?
Sickle-cell disease is an inherited blood disorder in which red blood cells are abnormally shaped like a sickle or crescent, which decreases their ability to move through blood vessels smoothly.
Genome Engineering Paves the Way for Sickle Cell Cure
A team of physicians and laboratory scientists has taken a key step toward a cure for sickle cell disease, using CRISPR-Cas9 gene editing to fix the mutated gene responsible for the disease in stem cells from the blood of affected patients For the first time, they have corrected the mutation in a proportion of stem cells that is high enough to produce a substantial benefit in…
FDA approves first new drug in 20 years for sickle cell
The U.S. Food and Drug Administration has approved the first drug in nearly 20 years for sickle cell, an inherited disease in which abnormally shaped red blood cells can't properly carry oxygen throughout the body,…
Genome engineering paves way for sickle cell cure
A team of physicians and laboratory scientists has taken a key step toward a cure for sickle cell disease, using CRISPR-Cas9 gene editing to fix the mutated gene responsible for the disease in stem cells from the blood of affected patients.
FDA Approves First New Drug For Sickle Cell In Nearly 20 Years
The U.S. Food and Drug Administration has approved the first drug in nearly 20 years for sickle cell, an inherited...
Sickle Cell Disease 101
In Houston alone, 50 babies are diagnosed with sickle cell disease every year and 800 to 1,000 are followed by Texas Children’s Hospital and Baylor College of Medicine physicians. More public awareness and education about sickle cell disease is critically important. Although many are aware of the disease, the causes, effects and treatment aren’t widely understood.
What is Sickle Cell Disease?
Sickle cell disease is a group of inherited blood ailments that affect the body’s red blood cell. It is a collection of disorders that makes the red blood cell to become sickle shaped.
What Is Sickle Cell Disease?
Sickle cell anemia affects the red blood cells. About one in every 600 Blacks is born with sickle cell, and one in 12 blacks carry the sickle cell trait. But what is sickle cell anemia? Like what y…
Sickle Cell: What to Look For
Sickle-cell is a form of anemia, meaning that there are not enough red blood cells to properly carry needed oxygen around the body. This results in a varie
What Is Sickle-Cell Anemia?
The hereditary condition known as sickle-cell anemia affects about 72,000 people. It is most common in African Americans, occurring in around one in 500 bi